Ty Sperle says he felt "insane shock" after learning he'd been cured of a rare genetic disease through a clinical trial using a new gene-editing treatment.

KJ Muldoon, the first infant to undergo gene-editing therapy, has accomplished another first as a 1-year-old — his first steps KJ is walking at home ahead of Christmas after being hospitalized last ...

SHANGHAI, Nov. 5, 2025 /PRNewswire/ -- On November 6, 2025, Shanghai, China, CorrectSequence Therapeutics Co., Ltd. (Correctseq), a clinical-stage biotechnology company pioneering transformer Base ...

Prime Medicine said it has gained FDA clearance for the first human trials of a prime editing therapy as the agency has approved an investigational new drug (IND) application for the company’s first ...

There's new hope this week for people who suffer from sickle cell disease. The Food and Drug Administration approved the first genetic treatments for the brutal blood disorder on Friday. The ...

SAN FRANCISCO—Prime Medicine is on track to file the first IND/CTA application for human trials of a prime editing therapy to the FDA during the first half of this year, with the first clinical data ...

The FDA approved the genetic therapies for anyone 12 and older suffering from the most severe form of sickle cell disease, a brutal blood disorder that has long been neglected by medical research. The ...

For the first time, researchers have produced evidence that gene-editing can cut high cholesterol, a major risk factor for the nation's leading killer. Preliminary results from a study involving 10 ...

Rachael has a degree in Zoology from the University of Southampton, and specializes in animal behavior, evolution, palaeontology, and the environment.View full profile Rachael has a degree in Zoology ...